Science | Researchers cure a genetic disease in unborn mice
by Julie Borg
Posted 8/13/18, 12:41 pm
Each year an estimated 8 million children are born worldwide with severe genetic disorders. During pregnancy, genetic disorders can impair fetal development and lead to birth defects, but currently no approved medical treatments exist to correct gene mutations before birth.
Now, in a study published on June 26 in Nature Communications, researchers from Carnegie Mellon and Yale universities used a unique gene modification method to correct gene mutations in mice early in embryonic development.